Gene Therapy lets Hemophiliacs to Skip Weekly Shots in Study

Medical researchers in Britain have successfully treated six patients suffering from the blood-clotting disease known as hemophilia B by injecting them with the correct form of a defective gene, a landmark achievement in the troubled field of gene therapy.

Hemophilia B, which was carried by Queen Victoria and affected most of the royal houses of Europe, is the first well-known disease to appear treatable by gene therapy, a technique with a 20-year record of almost unbroken failure.

A virus carrying a replacement gene for blood clotting was used by University College London researchers to help six patients.

“I think this is a terrific advance for the field

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Categories: Genetics, Health

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